Rare Drug Development Symposium 2023: Collaborate: Go Farther, Together

Create A Comprehensive Research Strategy
Understand the end-to-end process of drug discovery and development for rare disease and participate in a workshop where you’ll analyze your community’s potential and needs.

Leverage the Power of Data
What makes data valid and reliable? Once you have invested in a registry, what partnership models can  help you move the needle toward translational research?

Use AI for Drug Discovery and Repurposing
Find out how artificial intelligence is being used to transform an often complex, decades-long-mission into a more efficient process, reducing the timeline and cost to bring therapies to patients.

Understand Regulatory Considerations
Whether your organization is local or global, regulatory guidelines must be taken into account at each step. Learn how to navigate the requirements through case studies and expert advice.

Who should attend:

• Patient Advocacy Group leaders
• Patients
• Members of the rare disease community who want to learn more about the drug development process, the unique ways this applies to the development of therapeutics for rare diseases, and how they can engage with the process
• Clinicians and researchers focused on rare disease therapeutic targets

View 2022 Highlights

To learn more about the 2022 Symposium, read the summary report here. We look forward to seeing you at the 2023 Symposium.

A Year-Long Initiative in Rare Drug Development

In addition to activities surrounding the RARE Drug Development Symposium in June, Global Genes is providing educational resources to help advocates and organizations become better equipped to work with researchers and industry partners throughout the drug development process. This includes:

Rare Research Roadmap: This toolkit was designed to help advocates, individuals, families, and organizations better understand some of the potential routes to treatment and some of the key concepts that are part of these processes to work with researchers and industry partners throughout the drug development process.